9/07/2011 PERMALINK
Gene therapy cures 14 of 16 kids with "bubble boy disease". Nine years after getting gene therapy for a rare, inherited immune system disorder often called "bubble boy disease," 14 out of 16 children have been cured, researchers report. “These children, who would have died very young without treatment, are participating in life as fully as their brothers and sisters,” researcher H. Bobby Gaspar, MD, PhD recently told the health web site WebMD.